Archives
The State of Gene Targeted Therapies
How these promising therapies are being studied and tested for neuromuscular diseases
Tags: Drug Development, Featured Content, Gene Therapy, MDA Clinical and Scientific Conference, Research
Pushing Limits
A hiker proves she is stronger than FSHD by taking on the toughest trek of her life
Tags: From Where I Sit, Staying Active
Ongoing Clinical Trials
Updates on some of the most promising studies
Tags: Clinical Trials, Drug Approval, Drug Development, Featured Content, Gene Therapy, MDA Clinical and Scientific Conference, Research
Guiding Treatment for Myotonic Dystrophy
A Q&A with neurologist Tetsuo Ashizawa, M.D.
Tags: Gene Therapy, Research, Spotlight
From Drug Discovery to Delivery
FDA Panel (left to right): Janet Woodcock, MD, FDA Center for Drug Evaluation and Research, and Peter Marks, MD, PhD, FDA Center for Biologics Evaluation and Research. FDA directors and…
The Case for Newborn Screening
Identifying neuromuscular diseases at birth can yield great benefits but faces great challenges
Care Across the Lifespan
Addressing sensitive topics contributes to higher quality of life
Bennett Foundation Donates $500,000 to Orange, Calif., MDA Summer Camp
July 9 at the Irvine Ranch Outdoor Education Center in Orange, Calif., home to one of MDA’s nationwide Summer Camp programs, was a very good day. Campers and MDA staffers…
Tags: Summer Camp
2109 Clinical & Scientific Conference Highlight: Healthcare Technology Moves Out of the Clinic, Into the Pocket
Computers, laptops, tablets, and smartphones have become ubiquitous features of our daily lives — but not of our healthcare. At least, not yet. But a group of physicians at MDA’s…
2019 Clinical & Scientific Conference Highlight: What’s New in Neuromuscular Diseases?
At the 2019 MDA Clinical & Scientific Conference, one scientific session of interest centered on what’s new in neuromuscular diseases (NMDs). In this session, presenting scientists discussed progress in therapy…