Science + Research

Find the latest science and research updates as well as information to help you understand this ever-evolving field.

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Santhera Pharmaceuticals Releases Letter to DMD Community Announcing Temporary Suspension of Enrollment in BreatheDMD Expanded Access Program

By MDA Staff | November 26, 2019
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Roche Genentech Announces Positive Results from Pivotal Study of Risdiplam in SMA Types 2 and 3

By Jeanene Swanson | November 15, 2019
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Solid Biosciences Releases Letter to DMD Community Announcing Hold on IGNITE DMD Trial Due to a Serious Adverse Event

By MDA Staff | November 12, 2019
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Roche Genentech Releases Letter to DMD Community Announcing Discontinuation of Clinical Trials Program for DMD

By MDA Staff | November 6, 2019
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MDA Care Centers Combine Expert Care with Research, Clinical Trials, and Advanced Technology

By Jeanene Swanson | November 5, 2019
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AveXis Releases Letter to SMA Community: FDA Places Partial Hold on Clinical Trials for Intrathecally Delivered AVXS-101

By MDA Staff | November 1, 2019
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World Muscle Society Roundup: Clinical Trial Results of Treatments in Development for DMD, XLMTM, SMA, and Pompe Disease

By Jeanene Swanson | October 31, 2019
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Reata Pharmaceuticals Announces Positive Results from Pivotal Study of Omaveloxolone in FA

By Jeanene Swanson | October 30, 2019
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Capricor Therapeutics Announces Positive Interim Results from Phase 2 Study of CAP-1002 to Treat DMD

By Jeanene Swanson | October 29, 2019
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MDA Grants Charles Thornton More Than $1 Million in New Funding to Continue Supporting the Myotonic Dystrophy Clinical Research Network

By Jeanene Swanson | October 25, 2019