Science + Research

Find the latest science and research updates as well as information to help you understand this ever-evolving field.

An illustration of a doctor’s arm and hand holding tweezers and manipulating DNA.
Featured Article

Gene Editing Holds Promise as Viable Therapy

By Larry Luxner | November 18, 2024
A doctor wearing a white lab coat, face mask and gloves holds up a tablet showing the muscular system of the body. His face is not showing in the photo.
Featured Article

Understanding Myotonic Dystrophy (DM)

By Myrna Traylor | November 18, 2024
ALS - diagnosis written on a white piece of paper. Syringe and vaccine with drugs.
Blog Post

Behind the Drug: Tofersen (Qalsody) for ALS

By Larry Luxner | November 13, 2024
2024 Clinical and Scientific Conference - Mon 03042024
Blog Post

A Q&A Look into the Planning and Upcoming Topics of the 2025 MDA Clinical & Scientific Conference

By MDA Staff | November 6, 2024
Titled book Amyotrophic Lateral Sclerosis along with medical equipment, Title of book invented and fictitious made in Photoshop, conceptual image
Blog Post

Simply Stated: Updates in Amyotrophic Lateral Sclerosis (ALS)

By Sujatha Gurunathan | October 29, 2024
Blog Post

18th Annual MDA Night of Hope Gala Highlights the Byars Family’s ALS Journey and Honors Choate Construction

By Lisa Kirksey | October 3, 2024
Blog Post

Simply Stated: Updates in Charcot-Marie-Tooth Disease (CMT)

By Sujatha Gurunathan | September 26, 2024
Genetic engineeering concept with 3d rendering dna helix and a part of dna
Blog Post

Next-Generation Exon-Skipping Therapies May Change the DMD Landscape

By Myrna Traylor | September 13, 2024
2023 Clinical and Scientific Conference
Blog Post

MDA Kickstart: A New Hope for Ultra-Rare Neuromuscular Disease Treatments

By Sharon Hesterlee, Ph.D. | September 9, 2024
A father, mother, and three sons sit on an outdoor patio step
Blog Post

My Gene Therapy Journey: The Curran Family

By Rebecca Hume | September 5, 2024