Drug Development

Blog Post

Capricor Therapeutics Announces Positive Interim Results from Phase 2 Study of CAP-1002 to Treat DMD

By Jeanene Swanson | October 29, 2019
Blog Post

The ALS Association, ALS Finding A Cure, and MDA Co-Fund Clinical Trial Grant to Study Restoring Immune System Function to Treat ALS

By Jeanene Swanson | August 9, 2019
Blog Post

Scholar Rock Announces Positive Results from Phase 1 Study of SRK-015 to Treat SMA

By Jeanene Swanson | August 7, 2019
Blog Post

MDA Awards Venture Philanthropy Funding to Rachelle Crosbie to Develop a Novel Membrane-Stabilizing Drug for DMD

By Jeanene Swanson | July 18, 2019
Featured Article

From Drug Discovery to Delivery

By MDA Staff | July 15, 2019
Featured Article

Ongoing Clinical Trials

By Ori Rokach | July 15, 2019
Featured Article

The State of Gene Targeted Therapies

By Jeanene Swanson | July 15, 2019
Picture of two hands using a screwdriver to disassemble a strand of DNA
Featured Article

These 7 Things Can Help You Understand Gene Targeting Therapy

By Amy Madsen | July 15, 2019
Blog Post

2019 Clinical & Scientific Conference Highlight: What’s New in Neuromuscular Diseases?

By Jeanene Swanson | July 10, 2019
Blog Post

MDA Awards Venture Philanthropy Funding to Locana to Develop Novel Treatment for DM

By Jeanene Swanson | June 12, 2019