Drug Development

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Celebrating 25 Years of Impact: MDA’s Wings Over Wall Street Gala Honors Leaders in ALS Research and Advocacy

By MDA Staff | March 16, 2025
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Quest Podcast: PJ’s Protocol: A Lifesaving Procedure Fueled by Love

By MDA Staff | March 6, 2025
Composite image of scientific lab instruments: a microscope, a pipette, petri dishes, and a computer keyboard.
Featured Article

Innovations in GNE Myopathy Research

By Amy Bernstein | February 28, 2025
Creatine kinase (CK), also known as creatine phosphokinase (CPK) or phosphocreatine kinase, is an enzyme expressed by various tissues and cell types. CK catalyses the conversion of creatine and uses adenosine triphosphate (ATP) to create phosphocreatine (PCr) and adenosine diphosphate (ADP). This CK enzyme reaction is reversible and thus ATP can be generated from PCr and ADP.
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Simply Stated: RNA-Based Therapies in Development for Myotonic Dystrophy

By Sujatha Gurunathan | January 30, 2025
A researcher in a white lab coat with long brown hair rests her chin on her hand next to a computer with science research on the screen
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Innovative Research: Spotlight on MDA Research Grant Recipients

By Larry Luxner | December 20, 2024
Medical Research Scientist Working on Desktop Computer with Gene Analysis Software in Modern Science Research Laboratory. Lab Engineers in White Coats Conduct Experiments in the Background.
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Simply Stated: Emerging Therapies to Treat DMD

By Sujatha Gurunathan | December 20, 2024
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In Case You Missed It…

By MDA Staff | December 8, 2024
A young boy in a batman t shirt holds up a sign that says HOPE in front of a red curtain
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MDA CEO and President Dr. Wood Reflects on 2024: A Year of Milestones and Momentum

By Donald S. Wood, Ph.D., President and CEO, Muscular Dystrophy Association | December 5, 2024
ALS - diagnosis written on a white piece of paper. Syringe and vaccine with drugs.
Blog Post

Behind the Drug: Tofersen (Qalsody) for ALS

By Larry Luxner | November 13, 2024
Titled book Amyotrophic Lateral Sclerosis along with medical equipment, Title of book invented and fictitious made in Photoshop, conceptual image
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Simply Stated: Updates in Amyotrophic Lateral Sclerosis (ALS)

By Sujatha Gurunathan | October 29, 2024