Drug Development

ALS - diagnosis written on a white piece of paper. Syringe and vaccine with drugs.
Blog Post

Behind the Drug: Tofersen (Qalsody) for ALS

By Larry Luxner | November 13, 2024
Titled book Amyotrophic Lateral Sclerosis along with medical equipment, Title of book invented and fictitious made in Photoshop, conceptual image
Blog Post

Simply Stated: Updates in Amyotrophic Lateral Sclerosis (ALS)

By Sujatha Gurunathan | October 29, 2024
Genetic engineeering concept with 3d rendering dna helix and a part of dna
Blog Post

Next-Generation Exon-Skipping Therapies May Change the DMD Landscape

By Myrna Traylor | September 13, 2024
2023 Clinical and Scientific Conference
Blog Post

MDA Kickstart: A New Hope for Ultra-Rare Neuromuscular Disease Treatments

By Sharon Hesterlee, Ph.D. | September 9, 2024
wooden blocks spell out the word content with word bubbles above that say news and stories and photos and blog
Blog Post

In Case You Missed It…

By MDA Staff | September 8, 2024
A father, mother, and three sons sit on an outdoor patio step
Blog Post

My Gene Therapy Journey: The Curran Family

By Rebecca Hume | September 5, 2024
Illustration of a man walking into a DNA helix-shaped hedge maze.
Featured Article

Are You Ready for Gene Therapy? Here’s What You Need to Know

By Larry Luxner | August 13, 2024
Parents hold their four-year-old daughter, who received Zolgensma for spinal muscular atrophy as an infant.
Blog Post

A Revolutionary Decade for Spinal Muscular Atrophy Therapies

By Chris Anselmo | August 1, 2024
Blog Post

MDA Ambassador Guest Blog: Finding Hope and Optimism in New Treatments

By Chase Rankin | June 4, 2024
Woman in electric wheelchair waits for consultation with doctor in clinic waiting area. Nurse invites patient with disability on procedures. Medical staff and people in modern medical facility lobby.
Blog Post

Treatment Options for Autoimmune Neuromuscular Diseases

By Patrick Sullivan | May 17, 2024