Drug Development

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Clinical Trial Alert: Phase 3 Study of Brepocitinib in Adults with Dermatomyositis

By Sujatha Gurunathan | November 16, 2023
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AGAMREE ® (Vamorolone), Now FDA-Approved, Offers Hope for Children Living with Duchenne Muscular Dystrophy

By MDA Staff | October 26, 2023
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Clinical Trial Alert: Phase 3 Study of Batoclimab in Adults with MG

By Sujatha Gurunathan | September 29, 2023
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New Therapy Brings Hope for Late-Onset Pompe Disease

By Melissa Donahue | September 21, 2023
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Deconstructing SMA Types and Treatments

By Sujatha Gurunathan | August 23, 2023
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FDA Approves Sarepta’s ELEVIDYS for Treatment of DMD

By Sujatha Gurunathan | June 22, 2023
Featured Article

Gene Therapy Options Grow With New Drug Approvals

By Larry Luxner | May 18, 2023
Featured Article

How MDA Invests in Research Success

By Maggie Callahan | May 18, 2023
A female doctor or nurse concentrates while reviewing at a patient's test results.
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The Value of Natural History Studies for Neuromuscular Disease

By Sujatha Gurunathan | May 4, 2023
Motor neuron connecting to muscle fiber, 3D illustration. A neuromuscular junction allows the motor neuron to transmit a signal to the muscle causing contraction. It is affected by toxins and diseases
Blog Post

Simply Stated: Research Updates in Emery-Dreifuss Muscular Dystrophy (EDMD)

By Sujatha Gurunathan | April 28, 2023