Innovation

FDA Approves Alexion’s Ultomiris for Treatment of gMG

By Sujatha Gurunathan | April 28, 2022
Blog Post

Simply Stated: Inclusion Body Myositis, Revisited

By Sujatha Gurunathan | April 27, 2022
Blog Post

Natural History Trial of BMD Now Enrolling

By Sujatha Gurunathan | April 15, 2022
Blog Post

Promoting Diversity in Rare Disease Research

By Larry Luxner | April 8, 2022
Blog Post

Simply Stated: What is Myotonic Dystrophy?

By Sujatha Gurunathan | March 24, 2022
Clinical & Scientific Conference
Blog Post

2022 Clinical & Scientific Conference: March 16 Highlights

By Sujatha Gurunathan | March 16, 2022
Blog Post

2022 Clinical & Scientific Conference March 15 Highlights

By Sujatha Gurunathan | March 15, 2022
Clinical & Scientific Conference
Blog Post

2022 Clinical & Scientific Conference March 14 Highlights

By Sujatha Gurunathan | March 14, 2022
Blog Post

Clinical Trial Alert: Phase 1b/2a Study of WVE-N531 in a Subset of People Living with DMD

By Sujatha Gurunathan | March 11, 2022
Featured Article

A New Direction for Charcot-Marie-Tooth Disease

By MDA Staff | February 16, 2022