Innovation

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Biogen’s Early Access Program for Tofersen is Now Open for Individuals with Rapidly Progressing SOD1-ALS

By Sujatha Gurunathan | July 6, 2021
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Expanding Knowledge on GNE Myopathy

By MDA Staff | May 14, 2021
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How Viral Vectors Deliver the Goods in Gene Therapy

By Larry Luxner | May 14, 2021
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FDA Approves Sarepta Therapeutics’ Amondys 45 for Treatment of DMD Amenable to Skipping Exon 45

By Sujatha Gurunathan | February 25, 2021
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Once a Wild Idea, Successful First-Generation Exon-Skipping Therapies Pave the Way for Personalized Treatments

By Sujatha Gurunathan | November 17, 2020
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Look & Feel Your Best During Stressful Times: Tips From a Disability Fashion Blogger

By Lainie Ishbia | September 3, 2020
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FDA Accepts Sarepta Therapeutics’ New Drug Application for DMD Treatment Casimersen

By Sujatha Gurunathan | August 26, 2020
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A Q&A With MDA Let’s Play Community Manager Paul Scherer

By Lindsey Baker | July 15, 2020
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7 Ways to Make Life at Home Easier

By MDA Staff | May 15, 2020
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More Than a Game

By MDA Staff | October 11, 2019