Research Advances

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AGAMREE ® (Vamorolone), Now FDA-Approved, Offers Hope for Children Living with Duchenne Muscular Dystrophy

By MDA Staff | October 26, 2023
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Clinical Trial Alert: Phase 2/3 Study of an Investigational Medication in Pediatric Patients with Generalized Myasthenia Gravis

By Sujatha Gurunathan | October 4, 2023
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Clinical Trial Alert: Phase 3 Study of Batoclimab in Adults with MG

By Sujatha Gurunathan | September 29, 2023
Young disabled man in wheelchair doing strength exercises for hands in the rehabilitation clinic. Doctor physiotherapist helping him
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Simply Stated: Research Updates in Periodic Paralysis

By Sujatha Gurunathan | September 25, 2023
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Research Study Alert: Observational Study of Cardiovascular Function in Children with BMD or DMD

By Sujatha Gurunathan | September 22, 2023
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New Therapy Brings Hope for Late-Onset Pompe Disease

By Melissa Donahue | September 21, 2023
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Deconstructing SMA Types and Treatments

By Sujatha Gurunathan | August 23, 2023
Medical illustration about Sacrum.3d rending.
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Simply Stated: Research Updates in Spinal-Bulbar Muscular Atrophy (SBMA)

By Sujatha Gurunathan | August 1, 2023
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FDA Approves Sarepta’s ELEVIDYS for Treatment of DMD

By Sujatha Gurunathan | June 22, 2023
Featured Article

Gene Therapy Options Grow With New Drug Approvals

By Larry Luxner | May 18, 2023