Research Advances

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FDA Approves Sarepta’s ELEVIDYS for Treatment of DMD

By Sujatha Gurunathan | June 22, 2023
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Gene Therapy Options Grow With New Drug Approvals

By Larry Luxner | May 18, 2023
A female doctor or nurse concentrates while reviewing at a patient's test results.
Blog Post

The Value of Natural History Studies for Neuromuscular Disease

By Sujatha Gurunathan | May 4, 2023
FDA approved Biogen’s Qalsody for treatment of SOD1-ALS.
Blog Post

FDA Approves Biogen’s Qalsody for Treatment of SOD1-ALS

By Sujatha Gurunathan | April 25, 2023
Banner announcing the Pompe Disease Symposium, with speaker Priya Kishnani, MD, MBBS, at the 2023 MDA Clinical & Scientific Conference in Dallas, Texas. Photo Credit Larry Luxner
Blog Post

At MDA Conference, Pompe Disease Researchers Stressed Importance of Newborn Screening

By Larry Luxner | April 14, 2023
Blog Post

Quest Podcast: The Changing Landscape of Neuromuscular Care

By MDA Staff | March 15, 2023
Blog Post

FDA Approves Reata’s SKYCLARYS for Treatment of FA

By Sujatha Gurunathan | February 28, 2023
Closeup of an unclothed infant lying on its side on a white blanket while an adult hand holds a stethoscope to its chest.
Featured Article

Q&A: Understanding Congenital Muscular Dystrophy

By MDA Staff | February 16, 2023
Scientist examines DNA models on a lab screen
Blog Post

Simply Stated: Updates in Oculopharyngeal Muscular Dystrophy (OPMD)

By Sujatha Gurunathan | January 26, 2023
3 separate human skeletal clipart images are set in blue: a hand, with a red target indicating wrist contractures; a bent elbow, with a red target indicating elbow contractures; and a foot, with a red target indicating ankle contractures.
Featured Article

Q&A: Understanding Bethlem Myopathy

By MDA Staff | November 18, 2022