Research Advances

Featured Article

Researchers Want to Know More About Oculopharyngeal Muscular Dystrophy

By MDA Staff | August 20, 2021
Blog Post

FDA Approves Sanofi Genzyme’s Nexviazyme for Treatment of Pompe Disease

By MDA Staff | August 6, 2021
Blog Post

FDA approves Octapharma’s Octagam® 10% for Treatment of Adults with Dermatomyositis

By Sujatha Gurunathan | July 29, 2021
Blog Post

Biogen’s Early Access Program for Tofersen is Now Open for Individuals with Rapidly Progressing SOD1-ALS

By Sujatha Gurunathan | July 6, 2021
Featured Article

How Viral Vectors Deliver the Goods in Gene Therapy

By Larry Luxner | May 14, 2021
Featured Article

New Research Channels for Myotonia Congenita

By MDA Staff | February 23, 2021
Featured Article

The Search for Inclusion Body Myositis Treatment

By MDA Staff | December 4, 2020
Blog Post

Once a Wild Idea, Successful First-Generation Exon-Skipping Therapies Pave the Way for Personalized Treatments

By Sujatha Gurunathan | November 17, 2020
Blog Post

Scholar Rock Announces Positive Results from Interim Analysis of TOPAZ Phase 2 Study of SRK-015 to Treat SMA

By Sujatha Gurunathan | October 28, 2020
Blog Post

Amylyx Announces More Results from Study of AMX0035 to Treat ALS

By Sujatha Gurunathan | October 19, 2020