Research Advances

Blog Post

Capricor Announces Positive Results from its Phase 2 Study of CAP-1002 to Treat DMD

By Sujatha Gurunathan | September 30, 2021
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One in a Million

By Debra Gordon | August 20, 2021
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Researchers Want to Know More About Oculopharyngeal Muscular Dystrophy

By MDA Staff | August 20, 2021
Blog Post

FDA Approves Sanofi Genzyme’s Nexviazyme for Treatment of Pompe Disease

By MDA Staff | August 6, 2021
Blog Post

FDA approves Octapharma’s Octagam® 10% for Treatment of Adults with Dermatomyositis

By Sujatha Gurunathan | July 29, 2021
Blog Post

Biogen’s Early Access Program for Tofersen is Now Open for Individuals with Rapidly Progressing SOD1-ALS

By Sujatha Gurunathan | July 6, 2021
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How Viral Vectors Deliver the Goods in Gene Therapy

By Larry Luxner | May 14, 2021
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New Research Channels for Myotonia Congenita

By MDA Staff | February 23, 2021
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The Search for Inclusion Body Myositis Treatment

By MDA Staff | December 4, 2020
Blog Post

Once a Wild Idea, Successful First-Generation Exon-Skipping Therapies Pave the Way for Personalized Treatments

By Sujatha Gurunathan | November 17, 2020