Clinical Trial Alert

Blog Post

Clinical Study Alert: Phase 1 Study of MyoPAXon in Boys with DMD

By MDA Staff | March 9, 2026
Blog Post

Clinical Research Alert: Phase 2 Study of Rapcabtagene Autoleucel in Individuals with IIM

By MDA Staff | March 6, 2026
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Clinical Research Alert: Observational Study in Female Carriers of DMD/BMD and Their Biological Children

By MDA Staff | March 5, 2026
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Clinical Research Alert: Phase 2 Study of NMD670 in Adults with Generalized Myasthenia Gravis (gMG)

By MDA Staff | March 2, 2026
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Clinical Research Alert: Phase 3 Study of Salanersen in Presymptomatic Newborns with SMA

By MDA Staff | January 15, 2026
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Clinical Research Alert: Phase 1 Study of Gene Therapy in Individuals with Myotonic Dystrophy Type 1

By MDA Staff | December 19, 2025
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Clinical Research Alert: Two Phase 4 Studies of Risdiplam in Pediatric SMA Patients Following Gene Therapy

By MDA Staff | December 17, 2025
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Clinical Research Alert: Phase 1/2 Study of DYNE-101 in Individuals with Myotonic Dystrophy Type 1

By MDA Staff | December 17, 2025
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Clinical Research Alert: Natural History Study of Individuals with Cardiomyopathy Associated with FRDA

By MDA Staff | November 21, 2025
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Clinical Research Alert: Real World Study of Male Fertility Following Risdiplam Treatment

By MDA Staff | November 19, 2025