Clinical Trial Alert

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Clinical Research Alert: Observational Study in Female Carriers of SMA and Their Biological Children

By MDA Staff | April 22, 2025
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Clinical Research Opportunity: LION-CS101 a Phase 1/2 Study of AB-1003 in Adults with LGMD2I/R9

By MDA Staff | March 31, 2025
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Clinical Trial Alert: Phase 2/3 Study of an Investigational Medication in Pediatric Patients with Generalized Myasthenia Gravis

By MDA Staff | February 19, 2025
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Clinical Trial Alert: Phase 2 Pivotal Study of Sevasemten (EDG-5506) in Adults with Becker Muscular Dystrophy

By Sujatha Gurunathan | June 17, 2024
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Clinical Study Alert: Open-Label, Observational Study of Risdiplam in Adults with SMA

By Sujatha Gurunathan | May 17, 2024
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Clinical Trial Alert: Phase 3 Study of ALXN1720 in Adults with Generalized Myasthenia Gravis (gMG)

By Sujatha Gurunathan | May 13, 2024
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Clinical Study Alert: Phase 2 Study of Vamorolone in Adults with BMD

By Sujatha Gurunathan | April 2, 2024
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Clinical Study Alert: Phase 2 Study of Brogidirsen in Boys with DMD

By Sujatha Gurunathan | March 29, 2024
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Clinical Study Alert: A Phase 1/2 Study of Safety and Efficacy of LX2006 Gene Therapy in Adults with Cardiomyopathy Associated with Friedreich Ataxia

By Sujatha Gurunathan | March 25, 2024
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Clinical Trial Alert: Medical Device Feasibility Study for People with ALS

By MDA Staff | December 21, 2023