Clinical Trials

Blog Post

Clinical Research Alert: Phase 1/2 Study of SGT-003 in Boys with DMD

By MDA Staff | September 2, 2025
Featured Article

Progress Now: Research News and Updates Across MDA Diseases

By MDA Staff | August 19, 2025
Graphic of laboratory equipment to signify neuromuscular disease research
Featured Article

Neuromuscular Disease Research: Going Strong

By Andrew Zaleski | August 19, 2025
Blog Post

Behind the Drug: Nusinersen (Spinraza) for SMA

By Maggie Callahan | August 6, 2025
Blog Post

Clinical Research Alert: At-Home Research Study in People with DM1

By MDA Staff | August 4, 2025
Woman in electric wheelchair waits for consultation with doctor in clinic waiting area. Nurse invites patient with disability on procedures. Medical staff and people in modern medical facility lobby.
Blog Post

Behind the Drug: Risdiplam (Evrysdi) for SMA

By Maggie Callahan | July 31, 2025
Blog Post

Clinical Research Alert: Phase 3 Study of RGX-202 in Boys with DMD

By MDA Staff | June 30, 2025
Disabled Father play with his little son on the playground
Blog Post

Your Guide to Genetic Testing for Neuromuscular Diseases

By Megan Kramer-Salvitti | June 20, 2025
3d illustration showing molecules passing an ion channel in cell membrane
Blog Post

Simply Stated: Updates in Ryanodine Receptor 1-Related Disorders (RYR-1-RD)

By Sujatha Gurunathan | May 29, 2025
Illustration of a researcher in a white lab coat climbing a ladder shaped like a DNA helix.
Featured Article

Why MDA’s Kickstart Program Is a Game-changer for Gene Therapies

By Amy Bernstein | May 23, 2025