Clinical Trials

Featured Article

Gene Therapy Options Grow With New Drug Approvals

By Larry Luxner | May 18, 2023
Two men in dark suit jackets and ties stand in front of a large blue screen with words projected on it: MDA Clinical & Scientific Conference.
Featured Article

2023 MDA Clinical & Scientific Conference Makes an Impact

By MDA Staff | May 18, 2023
A female doctor or nurse concentrates while reviewing at a patient's test results.
Blog Post

The Value of Natural History Studies for Neuromuscular Disease

By Sujatha Gurunathan | May 4, 2023
Motor neuron connecting to muscle fiber, 3D illustration. A neuromuscular junction allows the motor neuron to transmit a signal to the muscle causing contraction. It is affected by toxins and diseases
Blog Post

Simply Stated: Research Updates in Emery-Dreifuss Muscular Dystrophy (EDMD)

By Sujatha Gurunathan | April 28, 2023
Green background with word Clinical Trial Alert and a picture of scientists in a lab
Blog Post

Clinical Trial Alert: Phase 3 Study of Pozelimab and Cemdisiran in Adults with gMG

By Sujatha Gurunathan | April 26, 2023
FDA approved Biogen’s Qalsody for treatment of SOD1-ALS.
Blog Post

FDA Approves Biogen’s Qalsody for Treatment of SOD1-ALS

By Sujatha Gurunathan | April 25, 2023
Digital background depicting innovative technologies in genetic research
Blog Post

Simply Stated: Research Updates in Pompe Disease

By Sujatha Gurunathan | March 29, 2023
Blog Post

2023 MDA Clinical and Scientific Conference Starts Strong

By Amy Bernstein | March 21, 2023
Clinical Trial Alert with image of researcher's gloved hand holding a test tube
Blog Post

Clinical Trial Alert: Phase 2 Study of ALXN2050 in Adults with Generalized Myasthenia Gravis (gMG)

By Sujatha Gurunathan | March 9, 2023
Men's hand arranging front view wood blocks with healthcare medicine icons
Blog Post

What About My Disease? Why a New Treatment for One Neuromuscular Disease Is Good News for All

By Cheryl Alkon | February 27, 2023