Clinical Trials

Blog Post

FDA Approves Jacobus Pharmaceuticals’ Ruzurgi for Treatment of Children with Lambert-Eaton Myasthenic Syndrome

By Jeanene Swanson | May 8, 2019
Blog Post

Progress in Motion: MDA’s 2019 Clinical & Scientific Conference Heralds New Directions for Neuromuscular Disease Treatment

By MDA Staff | May 3, 2019
Blog Post

Biogen Releases Letter to ALS Community

By MDA Staff | May 2, 2019
Blog Post

Clinical Trial Alert: PTC Therapeutics Seeks Participants for a Phase 3 DMD Study

By MDA Staff | April 24, 2019
Blog Post

Sarepta Therapeutics Announces Positive Interim Results from Study of Casimersen to Treat DMD Amenable to Exon 45 Skipping

By Jeanene Swanson | April 4, 2019
Blog Post

FDA Grants Orphan Drug Designation to Acceleron Pharma’s ACE-083 Muscle Growth Drug for Charcot-Marie-Tooth Disease

By Jeanene Swanson | April 3, 2019
Blog Post

Clinical Trial Alert: Researchers at Neurogene Seek Participants for a CMT4J Natural History Study

By MDA Staff | March 21, 2019
Blog Post

Sarepta Therapeutics Announces Positive Interim Results in Gene Therapy Trial for LGMD2E and Acquisition of Myonexus Therapeutics

By Jeanene Swanson | March 15, 2019
Blog Post

Clinical Trial Alert: ReveraGen BioPharma Seeks Participants for a Phase 2b DMD Study

By MDA Staff | March 12, 2019
Blog Post

FDA Grants Breakthrough Therapy Designation to Amicus’ Experimental Therapy, AT-GAA, for Late-Onset Pompe Disease

By Jeanene Swanson | March 7, 2019