Gene Therapy

Collage image with six photos of various MDA events and supported research
Blog Post

2023 in Review: A Letter from MDA President and CEO, Dr. Wood

By Donald S. Wood, Ph.D., President and CEO, Muscular Dystrophy Association | December 11, 2023
wooden blocks spell out the word content with word bubbles above that say news and stories and photos and blog
Blog Post

In Case You Missed It…

By MDA Staff | October 6, 2023
A family poses with Disney's Pluto
Blog Post

Insurance Denials for Gene Therapy Treatment Delay Access to Care

By Rebecca Hume | September 29, 2023
A young girl with blonde hair sitting on a doctor’s table as a doctor, a woman with brown hair, uses a reflex hammer on the girl’s knee. Both girl and doctor are smiling.
Featured Article

Advances in the Treatment of Friedreich Ataxia

By MDA Staff | August 8, 2023
Scientist examines DNA models in modern Genetic Research Laboratory.
Blog Post

MDA’s Legislative Efforts to Increase Access to Genetic Medicine

By Joel Cartner | August 7, 2023
DNA spiral pill on black background. Genetically modified food concept.
Blog Post

DMD Gene Therapy Approval Ignites Hope

By Larry Luxner | August 1, 2023
Blog Post

FDA Approves Sarepta’s ELEVIDYS for Treatment of DMD

By Sujatha Gurunathan | June 22, 2023
Featured Article

Gene Therapy Options Grow With New Drug Approvals

By Larry Luxner | May 18, 2023
Two men in dark suit jackets and ties stand in front of a large blue screen with words projected on it: MDA Clinical & Scientific Conference.
Featured Article

2023 MDA Clinical & Scientific Conference Makes an Impact

By MDA Staff | May 18, 2023
Motor neuron connecting to muscle fiber, 3D illustration. A neuromuscular junction allows the motor neuron to transmit a signal to the muscle causing contraction. It is affected by toxins and diseases
Blog Post

Simply Stated: Research Updates in Emery-Dreifuss Muscular Dystrophy (EDMD)

By Sujatha Gurunathan | April 28, 2023