Gene Therapy

Illustration of a black metal pipeline on a yellow background
Featured Article

What Is the Drug Development Pipeline?

By Amy Bernstein | February 12, 2024
Blog Post

Announcing the 2024 MDA Clinical & Scientific Conference Agenda

By MDA Staff | January 11, 2024
Blog Post

9 Questions to Ask Before Joining a Clinical Trial

By Myrna Traylor | January 11, 2024
Collage image with six photos of various MDA events and supported research
Blog Post

2023 in Review: A Letter from MDA President and CEO, Dr. Wood

By Donald S. Wood, Ph.D., President and CEO, Muscular Dystrophy Association | December 11, 2023
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Blog Post

In Case You Missed It…

By MDA Staff | October 6, 2023
A family poses with Disney's Pluto
Blog Post

Insurance Denials for Gene Therapy Treatment Delay Access to Care

By Rebecca Hume | September 29, 2023
A young girl with blonde hair sitting on a doctor’s table as a doctor, a woman with brown hair, uses a reflex hammer on the girl’s knee. Both girl and doctor are smiling.
Featured Article

Advances in the Treatment of Friedreich Ataxia

By MDA Staff | August 8, 2023
Scientist examines DNA models in modern Genetic Research Laboratory.
Blog Post

MDA’s Legislative Efforts to Increase Access to Genetic Medicine

By Joel Cartner | August 7, 2023
DNA spiral pill on black background. Genetically modified food concept.
Blog Post

DMD Gene Therapy Approval Ignites Hope

By Larry Luxner | August 1, 2023
Blog Post

FDA Approves Sarepta’s ELEVIDYS for Treatment of DMD

By Sujatha Gurunathan | June 22, 2023