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Gene Therapy Options Grow With New Drug Approvals

By Larry Luxner | May 18, 2023
Two men in dark suit jackets and ties stand in front of a large blue screen with words projected on it: MDA Clinical & Scientific Conference.
Featured Article

2023 MDA Clinical & Scientific Conference Makes an Impact

By MDA Staff | May 18, 2023
Motor neuron connecting to muscle fiber, 3D illustration. A neuromuscular junction allows the motor neuron to transmit a signal to the muscle causing contraction. It is affected by toxins and diseases
Blog Post

Simply Stated: Research Updates in Emery-Dreifuss Muscular Dystrophy (EDMD)

By Sujatha Gurunathan | April 28, 2023
Banner announcing the Pompe Disease Symposium, with speaker Priya Kishnani, MD, MBBS, at the 2023 MDA Clinical & Scientific Conference in Dallas, Texas. Photo Credit Larry Luxner
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At MDA Conference, Pompe Disease Researchers Stressed Importance of Newborn Screening

By Larry Luxner | April 14, 2023
Digital background depicting innovative technologies in genetic research
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Simply Stated: Research Updates in Pompe Disease

By Sujatha Gurunathan | March 29, 2023
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2023 MDA Clinical and Scientific Conference Starts Strong

By Amy Bernstein | March 21, 2023
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Quest Podcast: The Changing Landscape of Neuromuscular Care

By MDA Staff | March 15, 2023
Men's hand arranging front view wood blocks with healthcare medicine icons
Blog Post

What About My Disease? Why a New Treatment for One Neuromuscular Disease Is Good News for All

By Cheryl Alkon | February 27, 2023
Closeup of an unclothed infant lying on its side on a white blanket while an adult hand holds a stethoscope to its chest.
Featured Article

Q&A: Understanding Congenital Muscular Dystrophy

By MDA Staff | February 16, 2023
Scientist examines DNA models on a lab screen
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Simply Stated: Updates in Oculopharyngeal Muscular Dystrophy (OPMD)

By Sujatha Gurunathan | January 26, 2023