Gene Therapy

Illustration of a scientist in a mask examining a sample with a microscope amid DNA, molecules, and laboratory equipment.
Featured Article

Understanding Myotubular Myopathy (MTM)

By Michelle Jackson | August 21, 2026
Researcher Asuka Eguchi in a white lab coat smiles while holding a pipette at a laboratory workstation.
Featured Article

From Research to Reality: Meet 2 Researchers Driving Drug Development Progress

By Janet Celosia | August 21, 2026
Doctor speaking with a child and caregiver in a medical office with a microscope on the desk.
Blog Post

New Myotubular Myopathy Clinical Trial May Lead to Safer Gene Therapy

By Amy Bernstein | August 13, 2026
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Blog Post

In Case You Missed It…

By MDA Staff | April 8, 2026
DNA molecule research study concept. The doctor makes manipulations with the DNA molecule on a blurred background.
Blog Post

Research Network Supports Limb-Girdle Muscular Dystrophy Treatment Development

By Amy Bernstein | March 4, 2026
Illustration of figures using scissors to cut a medical price tag into three pieces.
Featured Article

Expert Tips for Handling an Insurance Claim Denial for Gene Therapy

By Emily Blume | February 23, 2026
MDA Clinical & Scientific Conference attendees gather around a sign about MDA’s history supporting neuromuscular research.
Featured Article

MDA Clinical & Scientific Conference Sessions Drive Innovation in Neuromuscular Care

By Rene Ryan | February 23, 2026
A compass, with the needle pointing north, rests on a rocky shore.
Featured Article

The New Diagnostic Journey: Advances in Genetic Testing Speed Rare Disease Diagnosis

By Amy Bernstein | February 23, 2026
wooden blocks spell out the word content with word bubbles above that say news and stories and photos and blog
Blog Post

In Case You Missed It…

By MDA Staff | January 8, 2026
Illustration of a microscope and surrounded by beakers and test tubes.
Featured Article

Progress Now: Immunotherapy Study Recruiting, Drug Cleared for Expanded Access, and More

By MDA Staff | November 14, 2025