Research

A 3d rendering of a mitochondrion, the powerhouse of the cell, intertwined with a segment of DNA.
Blog Post

Simply Stated: Updates in Primary Mitochondrial Diseases

By Sujatha Gurunathan | November 26, 2025
Illustration of a microscope and surrounded by beakers and test tubes.
Featured Article

Progress Now: Immunotherapy Study Recruiting, Drug Cleared for Expanded Access, and More

By MDA Staff | November 14, 2025
Illustration of a DNA double helix on a dark blue background
Featured Article

Say Yes to Gene Therapy? Factors to Consider When Gene Therapy Is an Option

By Amy Bernstein | November 14, 2025
A group of scientists at the 2025 MDA Clinical & Scientific Conference, one way MDA fosters collaboration among experts across neuromuscular diseases.
Featured Article

MDA’s Umbrella of Care: One Organization Connecting 300+ Neuromuscular Diseases

By Michelle Jackson | November 12, 2025
Arturito Estopinan, a teen who received a new therapy for the rare TK2d disease, seated in a wheelchair between his parents, Olga and Art.
Blog Post

How Expanded Access and Compassionate Use Broaden Access to Investigational Therapies

By Amy Bernstein | November 4, 2025
Blog Post

Quest Podcast: Voices of Inclusion: Celebrating NDEAM with Disability:IN

By MDA Staff | October 21, 2025
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Blog Post

In Case You Missed It…

By MDA Staff | October 8, 2025
Blog Post

Quest Podcast: Precision Medicine: Mapping the Genetic Code for New Treatments

By MDA Staff | September 24, 2025
wooden blocks spell out the word content with word bubbles above that say news and stories and photos and blog
Blog Post

In Case You Missed It…

By MDA Staff | September 8, 2025
Featured Article

Progress Now: Research News and Updates Across MDA Diseases

By MDA Staff | August 19, 2025