Research

Priyanka Kakkar and Dr. Alan Beggs at a conference booth for Cure ADSSL1, an organization raising awareness and supporting research for ADSS1 myopathy.
Featured Article

Understanding ADSS1 or ADSSL1 Myopathy

By Michelle Jackson | May 26, 2026
Illustration of a microscope, beakers, and test tubes
Featured Article

Progress Now: Drug Approvals and Clinical Trial Updates

By MDA Staff | May 26, 2026
Detailed 3D illustration of a human heart with visible arteries and veins against a dark background.
Featured Article

New Cardiac Insights Show How Neuromuscular Diseases Affect the Heart

By Chris Anselmo | May 26, 2026
wooden blocks spell out the word content with word bubbles above that say news and stories and photos and blog
Blog Post

In Case You Missed It…

By MDA Staff | May 8, 2026
Pharmaceutical research and medical concepts
Blog Post

Beyond Approval: Why Drug Development Doesn’t End at FDA Sign-Off

By Megan Kramer-Salvitti | April 20, 2026
John Crowly stands at a podium in the spotlight in a dark auditorium. Signage on the podium and behind him says MDA Clinical and Scientific Conference.
Blog Post

Pompe Disease and the Real Story Behind Dr. Stonehill, John Crowley, and ‘Extraordinary Measures’

By Amy Bernstein (Updated) | April 13, 2026
John Crowly and Sharon Hesterlee having a sit-down conversation on stage at the 2026 MDA Clinical & Scientific Conference
Blog Post

2026 MDA Clinical & Scientific Conference Opening Highlights the Power of Collaboration

By Amy Bernstein | March 10, 2026
Blog Post

MDA Awards Honors Those Driving Progress in Neuromuscular Research and Care

By Amy Bernstein | March 6, 2026
DNA molecule research study concept. The doctor makes manipulations with the DNA molecule on a blurred background.
Blog Post

Research Network Supports Limb-Girdle Muscular Dystrophy Treatment Development

By Amy Bernstein | March 4, 2026
Human brain anatomy with Neurons, brain cells, neural network Synaptic transmission , Synapses. 3d illustration
Blog Post

Rare Disease Day: Momentum in Neuromuscular Diseases is Building, but Progress Depends on Sustained Investment

By Brian Lin, PhD | February 27, 2026