Research

Genetic engineeering concept with 3d rendering dna helix and a part of dna
Blog Post

Next-Generation Exon-Skipping Therapies May Change the DMD Landscape

By Myrna Traylor | September 13, 2024
2023 Clinical and Scientific Conference
Blog Post

MDA Kickstart: A New Hope for Ultra-Rare Neuromuscular Disease Treatments

By Sharon Hesterlee, Ph.D. | September 9, 2024
wooden blocks spell out the word content with word bubbles above that say news and stories and photos and blog
Blog Post

In Case You Missed It…

By MDA Staff | September 8, 2024
Illustration of a man walking into a DNA helix-shaped hedge maze.
Featured Article

Are You Ready for Gene Therapy? Here’s What You Need to Know

By Larry Luxner | August 13, 2024
Back view of african woman rubbing her inflamed neck and loins, grey background
Featured Article

Understanding Myositis

By Myrna Traylor | August 13, 2024
Parents hold their four-year-old daughter, who received Zolgensma for spinal muscular atrophy as an infant.
Blog Post

A Revolutionary Decade for Spinal Muscular Atrophy Therapies

By Chris Anselmo | August 1, 2024
Image of the United States Capitol Building
Blog Post

Federal Appropriations: MDA and Neuromuscular Disease Community Priorities

By Jori Houck | June 13, 2024
Woman in electric wheelchair waits for consultation with doctor in clinic waiting area. Nurse invites patient with disability on procedures. Medical staff and people in modern medical facility lobby.
Blog Post

Treatment Options for Autoimmune Neuromuscular Diseases

By Patrick Sullivan | May 17, 2024
A group of people from neuromuscular advocacy organizations gathered at the 2024 MDA Clinical & Scientific Conference.
Featured Article

Understanding Titinopathies

By Myrna Traylor | May 9, 2024
Ribonucleic acid strands consisting of nucleotides important for protein bio-synthesis - 3d illustration
Blog Post

Simply Stated: Updates in SELENON-Related Myopathy

By Sujatha Gurunathan | May 7, 2024