Clinical Trials

Blog Post

Clinical Research Opportunity: Phase 3 Study of Cladribine in People with Generalized Myasthenia Gravis (gMG)

By MDA Staff | November 12, 2025
Blog Post

Clinical Research Alert: Phase 1 Study of AMX0114 in Adults with ALS

By MDA Staff | November 11, 2025
Arturito Estopinan, a teen who received a new therapy for the rare TK2d disease, seated in a wheelchair between his parents, Olga and Art.
Blog Post

How Expanded Access and Compassionate Use Broaden Access to Investigational Therapies

By Amy Bernstein | November 4, 2025
Blog Post

Clinical Study Alert: Phase 2 Study of Brogidirsen in Boys with DMD

By MDA Staff | September 5, 2025
Blog Post

Clinical Research Alert: Phase 1/2 Study of SGT-003 in Boys with DMD

By MDA Staff | September 2, 2025
Featured Article

Progress Now: Research News and Updates Across MDA Diseases

By MDA Staff | August 19, 2025
Graphic of laboratory equipment to signify neuromuscular disease research
Featured Article

Neuromuscular Disease Research: Going Strong

By Andrew Zaleski | August 19, 2025
Blog Post

Behind the Drug: Nusinersen (Spinraza) for SMA

By Maggie Callahan | August 6, 2025
Blog Post

Clinical Research Alert: At-Home Research Study in People with DM1

By MDA Staff | August 4, 2025
Woman in electric wheelchair waits for consultation with doctor in clinic waiting area. Nurse invites patient with disability on procedures. Medical staff and people in modern medical facility lobby.
Blog Post

Behind the Drug: Risdiplam (Evrysdi) for SMA

By Maggie Callahan | July 31, 2025