Clinical Trials

Motor neuron connecting to muscle fiber, 3D illustration. A neuromuscular junction allows the motor neuron to transmit a signal to the muscle causing contraction. It is affected by toxins and diseases
Blog Post

Simply Stated: Research Updates in Emery-Dreifuss Muscular Dystrophy (EDMD)

By Sujatha Gurunathan | April 28, 2023
Green background with word Clinical Trial Alert and a picture of scientists in a lab
Blog Post

Clinical Trial Alert: Phase 3 Study of Pozelimab and Cemdisiran in Adults with gMG

By Sujatha Gurunathan | April 26, 2023
FDA approved Biogen’s Qalsody for treatment of SOD1-ALS.
Blog Post

FDA Approves Biogen’s Qalsody for Treatment of SOD1-ALS

By Sujatha Gurunathan | April 25, 2023
Digital background depicting innovative technologies in genetic research
Blog Post

Simply Stated: Research Updates in Pompe Disease

By Sujatha Gurunathan | March 29, 2023
Blog Post

2023 MDA Clinical and Scientific Conference Starts Strong

By Amy Bernstein | March 21, 2023
Clinical Trial Alert with image of researcher's gloved hand holding a test tube
Blog Post

Clinical Trial Alert: Phase 2 Study of ALXN2050 in Adults with Generalized Myasthenia Gravis (gMG)

By Sujatha Gurunathan | March 9, 2023
Men's hand arranging front view wood blocks with healthcare medicine icons
Blog Post

What About My Disease? Why a New Treatment for One Neuromuscular Disease Is Good News for All

By Cheryl Alkon | February 27, 2023
Closeup of an unclothed infant lying on its side on a white blanket while an adult hand holds a stethoscope to its chest.
Featured Article

Q&A: Understanding Congenital Muscular Dystrophy

By MDA Staff | February 16, 2023
Featured Article

MOVR Data Hub Aims to Improve Research and Care

By Amy Bernstein | February 16, 2023
3 separate human skeletal clipart images are set in blue: a hand, with a red target indicating wrist contractures; a bent elbow, with a red target indicating elbow contractures; and a foot, with a red target indicating ankle contractures.
Featured Article

Q&A: Understanding Bethlem Myopathy

By MDA Staff | November 18, 2022