Exon Skipping

Genetic engineeering concept with 3d rendering dna helix and a part of dna
Blog Post

Next-Generation Exon-Skipping Therapies May Change the DMD Landscape

By Myrna Traylor | September 13, 2024
A group of people from neuromuscular advocacy organizations gathered at the 2024 MDA Clinical & Scientific Conference.
Featured Article

Understanding Titinopathies

By Myrna Traylor | May 9, 2024
Illustration of a black metal pipeline on a yellow background
Featured Article

What Is the Drug Development Pipeline?

By Amy Bernstein | February 12, 2024
DNA spiral pill on black background. Genetically modified food concept.
Blog Post

DMD Gene Therapy Approval Ignites Hope

By Larry Luxner | August 1, 2023
Featured Article

How MDA Invests in Research Success

By Maggie Callahan | May 18, 2023
Closeup of an unclothed infant lying on its side on a white blanket while an adult hand holds a stethoscope to its chest.
Featured Article

Q&A: Understanding Congenital Muscular Dystrophy

By MDA Staff | February 16, 2023
Featured Article

Research Grants Create a Path to Progress

By Karen Doss Bowman | August 23, 2022
clinical-trial-alert-image
Blog Post

Clinical Trial Alert: Phase 2 Study of Oral Ifetroban in Individuals with DMD

By Sujatha Gurunathan | August 10, 2022
Scientific conference speakers
Featured Article

A Successful In-Person Conference

By MDA Staff | May 13, 2022
Clinical & Scientific Conference
Blog Post

2022 Clinical & Scientific Conference: March 16 Highlights

By Sujatha Gurunathan | March 16, 2022