Exon Skipping

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Closeup of an unclothed infant lying on its side on a white blanket while an adult hand holds a stethoscope to its chest.
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Q&A: Understanding Congenital Muscular Dystrophy

By MDA Staff | February 16, 2023
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Research Grants Create a Path to Progress

By Karen Doss Bowman | August 23, 2022
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Clinical Trial Alert: Phase 2 Study of Oral Ifetroban in Individuals with DMD

By Sujatha Gurunathan | August 10, 2022
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A Successful In-Person Conference

By MDA Staff | May 13, 2022
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2022 Clinical & Scientific Conference: March 16 Highlights

By Sujatha Gurunathan | March 16, 2022
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Clinical Trial Alert: Phase 1b/2a Study of WVE-N531 in a Subset of People Living with DMD

By Sujatha Gurunathan | March 11, 2022
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Simply Stated: What is Duchenne Muscular Dystrophy?

By Sujatha Gurunathan | February 16, 2022
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Muscular Dystrophy Association Awards 18 Grants Totaling Over $1.6 Million for Neuromuscular Disease Research

By Sujatha Gurunathan | November 5, 2021
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FDA Approves Sarepta Therapeutics’ Amondys 45 for Treatment of DMD Amenable to Skipping Exon 45

By Sujatha Gurunathan | February 25, 2021
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Once a Wild Idea, Successful First-Generation Exon-Skipping Therapies Pave the Way for Personalized Treatments

By Sujatha Gurunathan | November 17, 2020