My Gene Therapy Journey

Doctor speaking with a child and caregiver in a medical office with a microscope on the desk.
Blog Post

New Myotubular Myopathy Clinical Trial May Lead to Safer Gene Therapy

By Amy Bernstein | August 13, 2026
Illustration of a DNA double helix on a dark blue background
Featured Article

Say Yes to Gene Therapy? Factors to Consider When Gene Therapy Is an Option

By Amy Bernstein | November 14, 2025
A father, mother, and three sons sit on an outdoor patio step
Blog Post

My Gene Therapy Journey: The Curran Family

By Rebecca Hume | September 5, 2024
Illustration of a man walking into a DNA helix-shaped hedge maze.
Featured Article

Are You Ready for Gene Therapy? Here’s What You Need to Know

By Larry Luxner | August 13, 2024
A mom and dad hold their daughter and smile at her
Blog Post

My Gene Therapy Journey: The Graves Family

By Rebecca Hume | August 7, 2024
Bafus family photo of mom and dad each holding one small boy
Blog Post

My Gene Therapy Journey: The Bafus Family

By Rebecca Hume | July 9, 2024
A family poses with Disney's Pluto
Blog Post

Insurance Denials for Gene Therapy Treatment Delay Access to Care

By Rebecca Hume | September 29, 2023
Featured Article

Gene Therapy Options Grow With New Drug Approvals

By Larry Luxner | May 18, 2023
Blog Post

Quest Podcast: The Changing Landscape of Neuromuscular Care

By MDA Staff | March 15, 2023
Graphic of DNA double helix on top of scientist with gloved hand holding a test tube
Blog Post

Perspectives on Gene Therapy Products for Neuromuscular Disease

By Sujatha Gurunathan | December 19, 2022