Clinical Trials

Blog Post

Scholar Rock Announces Positive Results from Interim Analysis of TOPAZ Phase 2 Study of SRK-015 to Treat SMA

By Sujatha Gurunathan | October 28, 2020
Blog Post

Amylyx Announces More Results from Study of AMX0035 to Treat ALS

By Sujatha Gurunathan | October 19, 2020
Featured Article

Expanding Access to Genetic Testing

By Donna Albrecht | August 14, 2020
Featured Article

MDA’s 2020 Advocacy Agenda Update

By Mark Fisher | August 14, 2020
Blog Post

FDA Approves NS Pharma’s Viltepso for Treatment of DMD Amenable to Exon 53 Skipping

By MDA Staff | August 12, 2020
Blog Post

FDA Approves Genentech’s Evrysdi for Treatment of SMA in Pediatric and Adult Patients

By MDA Staff | August 7, 2020
Blog Post

Biogen Announces Positive Results from Phase 1/2 Study of Tofersen to Treat a Genetic Form of ALS

By Sujatha Gurunathan | July 14, 2020
Blog Post

How MDA is Supporting LGMD Research and Care in 2020

By MDA Staff | July 10, 2020
Blog Post

Sarepta Therapeutics Announces Positive Results from the SRP-9001 Gene Therapy Trial to Treat DMD

By Sujatha Gurunathan | June 22, 2020
Blog Post

Momenta Pharmaceuticals Announces Positive Results from Phase 2 Vivacity-MG Study of Nipocalimab for Treatment of Generalized Myasthenia Gravis

By Sujatha Gurunathan | June 18, 2020