Healthcare

Front view of medical diverse team pushing emergency stretcher bed in the corridor at hospital
Blog Post

Expert Advice for Preparing for Medical Emergencies with NMD

By Rebecca Hume | April 24, 2026
Pharmaceutical research and medical concepts
Blog Post

Beyond Approval: Why Drug Development Doesn’t End at FDA Sign-Off

By Megan Kramer-Salvitti | April 20, 2026
wooden blocks spell out the word content with word bubbles above that say news and stories and photos and blog
Blog Post

In Case You Missed It…

By MDA Staff | April 8, 2026
Blog Post

MDA Ambassador Guest Blog: Rurally Complicated

By Jenna Ryerson | April 2, 2026
Adrian Krainer, PhD
Blog Post

Letter from the Editor: How New Higher-Dose Regimen for Spinraza Brings More Hope

By Mindy Henderson | March 30, 2026
Blog Post

Life with Lily: Why an Expert Specialist is Crucial for Your Care

By Lily Sander | March 27, 2026
Human brain anatomy with Neurons, brain cells, neural network Synaptic transmission , Synapses. 3d illustration
Blog Post

Rare Disease Day: Momentum in Neuromuscular Diseases is Building, but Progress Depends on Sustained Investment

By Brian Lin, PhD | February 27, 2026
DNA Helix analysis visualization data, genome sequence ui screen, futuristic genetic engineering lab infographic interface, 3D biotechnology scan report dashboard, medical science technology backgound
Featured Article

What Is a VUS? Variants of Unknown Significance in Genetic Testing and Why They Matter

By Amy Bernstein | February 23, 2026
Illustration of figures using scissors to cut a medical price tag into three pieces.
Featured Article

Expert Tips for Handling an Insurance Claim Denial for Gene Therapy

By Emily Blume | February 23, 2026
Illustration of a cross-section of a mitochondria, a sausage-shaped organelle that contains strands of mitochondrial DNA.
Featured Article

Understanding Thymidine Kinase 2 Deficiency

By Michelle Jackson | February 23, 2026