News

Read the latest news about issues affecting the neuromuscular disease community.

Blog Post

Sarepta Therapeutics Announces Positive Interim Results in Gene Therapy Trial for LGMD2E and Acquisition of Myonexus Therapeutics

By Jeanene Swanson | March 15, 2019
Blog Post

Clinical Trial Alert: ReveraGen BioPharma Seeks Participants for a Phase 2b DMD Study

By MDA Staff | March 12, 2019
Blog Post

Wisconsin Sen. Tammy Baldwin Introduces Air Carrier Access Amendments Act

By Brittany Hernandez | March 12, 2019
Blog Post

FDA Grants Breakthrough Therapy Designation to Amicus’ Experimental Therapy, AT-GAA, for Late-Onset Pompe Disease

By Jeanene Swanson | March 7, 2019
Blog Post

In Their Shoes: 65 Years of IAFF’s Fight for MDA

By Lindsey Baker | March 5, 2019
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Clinical Trial Alert: Amicus Therapeutics Seeks Participants for a Phase 3 Late-Onset Pompe Disease Study

By MDA Staff | March 5, 2019
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CMTA and MDA Co-Fund Proof-of-Concept Study Using AAV Vector to Deliver Gene Replacement Therapy in X-linked Charcot-Marie-Tooth Disease

By Jeanene Swanson | March 1, 2019
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FDA Accepts Sarepta Therapeutics’ New Drug Application (NDA) for Golodirsen to Treat DMD Amenable to Exon 53 Skipping

By Jeanene Swanson | March 1, 2019
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MDA Releases New DMD Fact Sheet During Duchenne Muscular Dystrophy Awareness Week

By MDA Staff | February 13, 2019
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Long-Term Results of Extension Study Validate Surgery as a Treatment for Myasthenia Gravis

By Jeanene Swanson | February 12, 2019