Science + Research

Find the latest science and research updates as well as information to help you understand this ever-evolving field.

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Clinical Trial Alert: Amicus Therapeutics Seeks Participants for a Phase 3 Late-Onset Pompe Disease Study

By MDA Staff | October 16, 2019
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Clinical Trial Alert: Momenta Pharmaceuticals Seeks Participants for a Phase 2 Myasthenia Gravis Study

By MDA Staff | October 15, 2019
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NS Pharma Submits New Drug Application to FDA for Viltolarsen to Treat DMD Amenable to Exon 53 Skipping

By Jeanene Swanson | October 7, 2019
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At a Cedars-Sinai Care Center, Dr. Robert Baloh Looks Under — and Ahead of — the Microscope for CMT and ALS

By Lindsey Baker | October 1, 2019
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Five Questions with LGMD Researcher Martin Childers

By Jeanene Swanson | September 30, 2019
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MDA Awards Clinical Research Network Grant to CMT Researcher Michael Shy for Inherited Neuropathies Consortium

By Jeanene Swanson | September 27, 2019
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In a Letter to the Duchenne Community, Santhera Announces Positive Results of Phase 2 Vamorolone Study, EMA’s Review of Puldysa to Treat Symptoms of DMD

By MDA Staff | September 26, 2019
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Five Questions with Friedreich’s Ataxia Researcher Sanjay Bidichandani

By Jeanene Swanson | September 25, 2019
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Clinical Trial Alert: Italfarmaco Seeks Participants for a Phase 3 DMD Study

By MDA Staff | September 25, 2019
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Researcher with CMT Awarded MDA Funding to Discover Rare Variants for Multiple Neuromuscular Diseases

By Jeanene Swanson | September 23, 2019