Antisense Oligonucleotide

A researcher in a white lab coat with long brown hair rests her chin on her hand next to a computer with science research on the screen
Blog Post

Innovative Research: Spotlight on MDA Research Grant Recipients

By Larry Luxner | December 20, 2024
Genetic engineeering concept with 3d rendering dna helix and a part of dna
Blog Post

Next-Generation Exon-Skipping Therapies May Change the DMD Landscape

By Myrna Traylor | September 13, 2024
Parents hold their four-year-old daughter, who received Zolgensma for spinal muscular atrophy as an infant.
Blog Post

A Revolutionary Decade for Spinal Muscular Atrophy Therapies

By Chris Anselmo | August 1, 2024
Illustration of a black metal pipeline on a yellow background
Featured Article

What Is the Drug Development Pipeline?

By Amy Bernstein | February 12, 2024
Featured Article

How MDA Invests in Research Success

By Maggie Callahan | May 18, 2023
Men's hand arranging front view wood blocks with healthcare medicine icons
Blog Post

What About My Disease? Why a New Treatment for One Neuromuscular Disease Is Good News for All

By Cheryl Alkon | February 27, 2023
Closeup of an unclothed infant lying on its side on a white blanket while an adult hand holds a stethoscope to its chest.
Featured Article

Q&A: Understanding Congenital Muscular Dystrophy

By MDA Staff | February 16, 2023
Featured Article

Research Grants Create a Path to Progress

By Karen Doss Bowman | August 23, 2022
Man in an electric wheelchair on a footpath in a suburban setting.
Featured Article

Understanding Amyotrophic Lateral Sclerosis

By MDA Staff | May 13, 2022
Featured Article

A Good Beginning: Newborn Screening

By Donna Albrecht | January 17, 2020