Research

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Capricor Announces Positive Results from its Phase 2 Study of CAP-1002 to Treat DMD

By Sujatha Gurunathan | September 30, 2021
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Scholar Rock Announces Positive Results from Interim Analysis of TOPAZ Phase 2 Study of SRK-015 to Treat SMA

By Sujatha Gurunathan | October 28, 2020
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FDA Approves NS Pharma’s Viltepso for Treatment of DMD Amenable to Exon 53 Skipping

By MDA Staff | August 12, 2020
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FDA Approves Genentech’s Evrysdi for Treatment of SMA in Pediatric and Adult Patients

By MDA Staff | August 7, 2020
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Biogen Announces Positive Results from Phase 1/2 Study of Tofersen to Treat a Genetic Form of ALS

By Sujatha Gurunathan | July 14, 2020
Dr. Stephan Züchner
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Five Questions With CMT Researcher Stephan Züchner

By MDA Staff | June 12, 2020
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Sarepta Therapeutics Announces Positive Results from the SRP-9003 Gene Therapy Trial to Treat LGMD2E

By Sujatha Gurunathan | June 11, 2020
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ReveraGen BioPharma Announces Completion of Vamorolone Study in 41 DMD Patients

By Sujatha Gurunathan | June 8, 2020
DNA strand and Cancer Cell Concept Science or medical background, 3d illustration.
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C9ORF72 Mutation Most Common Cause of Familial ALS, FTD, ALS-FTD

By Amy Madsen | September 20, 2011
View of armored military vehicle with dust surrounding it
Featured Article

ALS Research Poison Dirt

By Margaret Wahl | December 8, 2009