Gene Therapy

Featured Article

The Latest on Mitochondrial DNA Depletion Deletion Syndrome

By MDA Staff | November 19, 2021
Blog Post

Muscular Dystrophy Association Awards 18 Grants Totaling Over $1.6 Million for Neuromuscular Disease Research

By Sujatha Gurunathan | November 5, 2021
Featured Article

One in a Million

By Debra Gordon | August 20, 2021
Featured Article

Expanding Knowledge on GNE Myopathy

By MDA Staff | May 14, 2021
Featured Article

How Viral Vectors Deliver the Goods in Gene Therapy

By Larry Luxner | May 14, 2021
Featured Article

MDA Q A Top of Mind

By MDA Staff | May 14, 2021
Blog Post

How MDA is Supporting LGMD Research and Care in 2020

By MDA Staff | July 10, 2020
Blog Post

Sarepta Therapeutics Announces Positive Results from the SRP-9001 Gene Therapy Trial to Treat DMD

By Sujatha Gurunathan | June 22, 2020
Featured Article

MDA’s 2020 Clinical Scientific Conference Trial News and Updates

By MDA Staff | May 15, 2020
Featured Article

Pompe Disease Treatment Is Moving Forward

By MDA Staff | May 15, 2020