Gene Therapy

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MDA Q A Top of Mind

By MDA Staff | May 14, 2021
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How MDA is Supporting LGMD Research and Care in 2020

By MDA Staff | July 10, 2020
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Sarepta Therapeutics Announces Positive Results from the SRP-9001 Gene Therapy Trial to Treat DMD

By Sujatha Gurunathan | June 22, 2020
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MDA’s 2020 Clinical Scientific Conference Trial News and Updates

By MDA Staff | May 15, 2020
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Pompe Disease Treatment Is Moving Forward

By MDA Staff | May 15, 2020
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Antisense Therapeutics Announces Positive Results from Phase 2 Study of ATL1102 in DMD

By Jeanene Swanson | January 24, 2020
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MDA Awards More Than $1 Million in Venture Philanthropy Funding to AavantiBio to Develop Gene-Targeting Therapy for Friedreich’s Ataxia

By Jeanene Swanson | January 13, 2020
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Five Questions with DMD Researcher Matthew Wood

By Jeanene Swanson | October 23, 2019
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Five Questions with LGMD Researcher Martin Childers

By Jeanene Swanson | September 30, 2019
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Biogen Announces Positive Long-Term Results from Phase 2 Study of Spinraza to Treat SMA in Pre-Symptomatic Infants

By Jeanene Swanson | August 21, 2019