Gene Therapy

Featured Article

Expanding Knowledge on GNE Myopathy

By MDA Staff | May 14, 2021
Featured Article

How Viral Vectors Deliver the Goods in Gene Therapy

By Larry Luxner | May 14, 2021
Featured Article

MDA Q A Top of Mind

By MDA Staff | May 14, 2021
Blog Post

How MDA is Supporting LGMD Research and Care in 2020

By MDA Staff | July 10, 2020
Blog Post

Sarepta Therapeutics Announces Positive Results from the SRP-9001 Gene Therapy Trial to Treat DMD

By Sujatha Gurunathan | June 22, 2020
Featured Article

MDA’s 2020 Clinical Scientific Conference Trial News and Updates

By MDA Staff | May 15, 2020
Featured Article

Pompe Disease Treatment Is Moving Forward

By MDA Staff | May 15, 2020
Blog Post

Antisense Therapeutics Announces Positive Results from Phase 2 Study of ATL1102 in DMD

By Jeanene Swanson | January 24, 2020
Blog Post

MDA Awards More Than $1 Million in Venture Philanthropy Funding to AavantiBio to Develop Gene-Targeting Therapy for Friedreich’s Ataxia

By Jeanene Swanson | January 13, 2020
Blog Post

Five Questions with DMD Researcher Matthew Wood

By Jeanene Swanson | October 23, 2019