News

Read the latest news about issues affecting the neuromuscular disease community.

Blog Post

Clinical Trial Alert: Phase 2/3 and Open-Label Extension Study of ASP0367 in Individuals with Primary Mitochondrial Myopathy

By MDA Staff | August 9, 2021
Blog Post

FDA Approves Sanofi Genzyme’s Nexviazyme for Treatment of Pompe Disease

By MDA Staff | August 6, 2021
Blog Post

Research Study Alert: Survey for Caregivers of Children with SMA to Study Treatment Decision Making

By MDA Staff | July 30, 2021
Blog Post

Clinical Trial Alert: Phase 1b/2a Study of Descartes-08 in Adults with Generalized Myasthenia Gravis

By MDA Staff | July 30, 2021
Blog Post

FDA approves Octapharma’s Octagam® 10% for Treatment of Adults with Dermatomyositis

By Sujatha Gurunathan | July 29, 2021
Blog Post

Clinical Trial Alert: Phase 3 Study of Pamrevlumab (FG-3019) in Combination with Systemic Corticosteroids in Ambulatory Boys with DMD

By MDA Staff | July 25, 2021
Blog Post

Clinical Trial Alert: Phase 2 Study of Pitolisant for Treatment of Excessive Daytime Sleepiness in Adults with Myotonic Dystrophy, Type 1 (DM1)

By MDA Staff | July 16, 2021
Blog Post

Clinical Trial Alert: Phase 1b and Open-Label Extension Study of ASP0367 in Boys with DMD

By MDA Staff | July 15, 2021
Blog Post

Biogen’s Early Access Program for Tofersen is Now Open for Individuals with Rapidly Progressing SOD1-ALS

By Sujatha Gurunathan | July 6, 2021
Blog Post

Clinical Trial Alert: Phase 3 Study of Rozanolixizumab in Adults with Generalized Myasthenia Gravis

By MDA Staff | June 21, 2021