News

Read the latest news about issues affecting the neuromuscular disease community.

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Clinical Trial Alert: Amicus Therapeutics Seeks Participants for a Phase 3 Late-Onset Pompe Disease Study

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Clinical Trial Alert: Momenta Pharmaceuticals Seeks Participants for a Phase 2 Myasthenia Gravis Study

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Casey’s General Stores Round Up for MDA

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NS Pharma Submits New Drug Application to FDA for Viltolarsen to Treat DMD Amenable to Exon 53 Skipping

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MDA Awards Clinical Research Network Grant to CMT Researcher Michael Shy for Inherited Neuropathies Consortium

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In a Letter to the Duchenne Community, Santhera Announces Positive Results of Phase 2 Vamorolone Study, EMA’s Review of Puldysa to Treat Symptoms of DMD

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MDA Awards 25 Grants Totaling More Than $6.6 Million for Neuromuscular Disease Research

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Biogen Announces Positive Long-Term Results from Phase 2 Study of Spinraza to Treat SMA in Pre-Symptomatic Infants

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The ALS Association, ALS Finding A Cure, and MDA Co-Fund Clinical Trial Grant to Study Restoring Immune System Function to Treat ALS

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Scholar Rock Announces Positive Results from Phase 1 Study of SRK-015 to Treat SMA