Archives
Understanding Thymidine Kinase 2 Deficiency
Michio Hirano, MD, answers questions about TK2d, a rare mitochondrial myopathy with a new therapy approved by the FDA.
Tags: Drug Approval, Healthcare, MDA Care Centers, Research, Spotlight
RNA Therapies Offer Keys to Treating Genetic Neuromuscular Diseases
RNA therapies offer new hope for neuromuscular diseases, targeting faulty proteins without permanently altering DNA.
Young Leader Living with Muscular Dystrophy Champions Aiming High and Setting Goals
Caroline LeMay, a Harvard graduate living with a disability, knows the importance of education to achieve her dreams.
Tags: College, Education, Employment, Quest for Success, Young Adults
Progress Now: Research Updates and Breakthroughs
Tracking research updates and breakthroughs that help accelerate treatments and cures across MDA diseases.
Tags: Research, Research Advances
MDA Clinical & Scientific Conference Sessions Drive Innovation in Neuromuscular Care
Discoveries presented at the MDA Clinical & Scientific Conference can shape the future of neuromuscular care.
Community Members Share Their Everyday Milestones
MDA community members share meaningful moments and everyday milestones from the past year.
Sports, Disability, and Perseverance: How I Adapt to Stay in the Game
Trained sports broadcaster Michael Chamberlain has spent his career showing that people with disabilities belong in the sports world.
Tags: Employment, From Where I Sit, Young Adults
The New Diagnostic Journey: Advances in Genetic Testing Speed Rare Disease Diagnosis
New gene sequencing technologies mean better genetic testing, fewer delays in diagnosis, and more access to gene therapies.
Tags: Drug Development, Featured Content, Gene Therapy, Genetic Testing, Healthcare, Insurance, MDA Care Centers, Research, Technology
MDA Ambassador Guest Blog: The Secret to Navigating Life with a Rare Disease? Say Yes.
Charlotte is 11 years old and lives with LGMD2C, which was diagnosed when she was two and a half. When she grows up, Charlotte wants to get a law degree…
Tags: Ambassador Guest Blog, Ambassadors, Caregiving, Community, Mental Health, Relationships, Young Adults
Everything You Need to Know About the Upcoming 2026 MDA Clinical & Scientific Conference
The 2026 MDA Clinical & Scientific Conference is quickly approaching. Taking place March 8-11, 2026, at the Hilton Orlando in Orlando Florida, this year’s conference will explore the latest research…