Search Results: team momentum

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Blog Post | News, Science + Research

MDA Partners with the Broad Institute on Rare Genomes Project for Limb-Girdle Muscular Dystrophy

The Muscular Dystrophy Association (MDA) is pleased to announce a collaboration with the Broad Institute of MIT and Harvard, which aims to bring genetic diagnoses to more individuals living with…

Tags: Genetic Testing, Grants, Research


Blog Post | News, Science + Research

Muscular Dystrophy Association Bridges Clinical and Academic Neuromuscular Research for the First Time at Annual Meeting

With a laser focus on new horizons in neuromuscular research and care, the Muscular Dystrophy Association (MDA) is combining its clinical and scientific conferences for the first time, establishing a…

Tags: Gene Therapy, MDA Clinical and Scientific Conference, Newborn Screening, Research, Technology


Blog Post | News, Science + Research

Audentes Therapeutics Announces Plans to Develop Gene-Targeted Therapies for Duchenne Muscular Dystrophy and Myotonic Dystrophy Type 1

On April 8, Audentes Therapeutics announced that it will expand its gene-targeted therapy platform to include developing experimental drugs for Duchenne muscular dystrophy (DMD) and myotonic dystrophy type 1 (DM1).…

Tags: Antisense Oligonucleotide, Drug Development, Exon Skipping, Gene Therapy, Research


Blog Post | Personal Stories

A Tale of Two Siblings: Twin MDA Volunteers Forge Lifelong Connections — and Careers

Twin brother and sister Michael and Amy Schleicher’s story starts where a lot of kids’ stories do. They looked up to their big brother, Matt, and when he did something…

Tags: Community, MDA Care Centers, Muscle Walk, Summer Camp, Volunteers


Blog Post | News, Science + Research

Muscular Dystrophy Association Awards Eight Grants Totaling More Than $2 Million for ALS Research

Today, the Muscular Dystrophy Association (MDA) announced the awarding of eight new grants totaling more than $2 million toward research focused on amyotrophic lateral sclerosis (ALS), a disease in which…

Tags: Antisense Oligonucleotide, Drug Development, Gene Therapy, Grants, Research


Blog Post | News, Science + Research

Sarepta Therapeutics Announces Positive Interim Results from Study of Casimersen to Treat DMD Amenable to Exon 45 Skipping

On Mar. 28, Sarepta Therapeutics announced encouraging interim results from a phase 3 clinical trial that suggest the experimental drug casimersen potentially may be effective as a treatment for Duchenne muscular…

Tags: Clinical Trials, Drug Development, Exon Skipping, Gene Therapy


Blog Post | News, Science + Research

FDA Grants Orphan Drug Designation to Acceleron Pharma’s ACE-083 Muscle Growth Drug for Charcot-Marie-Tooth Disease

On Mar. 5, the U.S. Food and Drug Administration (FDA) awarded Orphan Drug designation to Acceleron Pharma’s ACE-083, a locally acting muscle agent, for treating Charcot-Marie-Tooth disease (CMT). Delivered by…

Tags: Clinical Trials, Drug Development, Research


Featured Article | Personal Stories

What Happened to You

A young man with SMA answers this question by becoming a student leader

Tags: College, College Experience, From Where I Sit, Young Adults


Featured Article | Science + Research

News on LEMS Treatment and Research

A Q&A with researcher Stephen Meriney, Ph.D.

Tags: Drug Approval, Drug Development, Grants, Research


Featured Article | Inclusion, Independence, Lifestyle

Making the Workplace Accessible

Think outside the cubicle to find solutions to common accessibility challenges in the office

Tags: Employment