Clinical Trials

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Santhera Pharmaceuticals Announces Publication of Positive Long-Term Results from Retrospective Study of Idebenone in DMD

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Solid Biosciences Releases Letter to DMD Community Announcing Update on IGNITE DMD Trial, Resolution of Serious Adverse Event

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Wave Life Sciences Releases Letter to DMD Community Announcing Discontinuation of Clinical Trials Program for Therapies Amenable to Skipping Exons 51 and 53

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Kadimastem Announces Positive Interim Results from Phase 1/2a Study of AstroRx in ALS

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FDA Accepts Roche Genentech’s NDA for Risdiplam for the Treatment of SMA

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Zogenix Announces Positive Results from Pivotal Study of Investigational Treatment MT1621 for TK2 Deficiency

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Santhera Pharmaceuticals Releases Letter to DMD Community Announcing Temporary Suspension of Enrollment in BreatheDMD Expanded Access Program

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Roche Genentech Announces Positive Results from Pivotal Study of Risdiplam in SMA Types 2 and 3

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What’s #GivingTuesday All About?

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Solid Biosciences Releases Letter to DMD Community Announcing Hold on IGNITE DMD Trial Due to a Serious Adverse Event