Duchenne Muscular Dystrophy (DMD)

Duchenne muscular dystrophy is a genetic disorder in which alterations of a protein called dystrophin lead to progressive muscle degeneration and weakness.

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Solid Biosciences Releases Letter to DMD Community Announcing Update on IGNITE DMD Trial, Resolution of Serious Adverse Event

By MDA Staff | December 18, 2019
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Wave Life Sciences Releases Letter to DMD Community Announcing Discontinuation of Clinical Trials Program for Therapies Amenable to Skipping Exons 51 and 53

By MDA Staff | December 16, 2019
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FDA Approves Sarepta Therapeutics’ Vyondys 53 for Treatment of DMD Amenable to Exon 53 Skipping

By Jeanene Swanson | December 13, 2019
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Santhera Pharmaceuticals Releases Letter to DMD Community Announcing Temporary Suspension of Enrollment in BreatheDMD Expanded Access Program

By MDA Staff | November 26, 2019
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Solid Biosciences Releases Letter to DMD Community Announcing Hold on IGNITE DMD Trial Due to a Serious Adverse Event

By MDA Staff | November 12, 2019
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Roche Genentech Releases Letter to DMD Community Announcing Discontinuation of Clinical Trials Program for DMD

By MDA Staff | November 6, 2019
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World Muscle Society Roundup: Clinical Trial Results of Treatments in Development for DMD, XLMTM, SMA, and Pompe Disease

By Jeanene Swanson | October 31, 2019
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Capricor Therapeutics Announces Positive Interim Results from Phase 2 Study of CAP-1002 to Treat DMD

By Jeanene Swanson | October 29, 2019
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Reporting Back from the MDA Public Policy and Advocacy Conference — and Keeping Up the Momentum

By Chris Anselmo | October 24, 2019
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Five Questions with DMD Researcher Matthew Wood

By Jeanene Swanson | October 23, 2019