Archives
2026 MDA Clinical & Scientific Conference Opening Highlights the Power of Collaboration
People from across the neuromuscular field gather to learn and collaborate at the 2026 MDA Clinical & Scientific Conference.
Clinical Study Alert: Phase 1 Study of MyoPAXon in Boys with DMD
Researchers at the University of Minnesota are seeking boys with Duchenne muscular dystrophy (DMD) to participate in a phase 1 clinical trial to evaluate the safety and efficacy of the investigational…
In Case You Missed It…
Quest Media is an innovative, adaptive lifestyle platform from MDA. With the power of this platform, we foster awareness and empowerment and have important conversations with experts, thought leaders, and…
MDA Ambassador Guest Blog: Redefining How I View Myself
Stephanie Chicas is 32 years old and lives in Alexandria, VA. Stephanie has SELENON congenital muscular dystrophy and uses a ventilator via a tracheostomy. She loves cuddling with her cat,…
Clinical Research Alert: Phase 2 Study of Rapcabtagene Autoleucel in Individuals with IIM
Researchers at Novartis are working to better understand idiopathic inflammatory myopathies (IIMs) and to evaluate a potential new treatment for individuals living with IIM who have not responded to previous treatments…
MDA Awards Honors Those Driving Progress in Neuromuscular Research and Care
Meet the 2026 MDA Legacy and Momentum award winners who are making a lasting impact on research and care for the neuromuscular community.
Clinical Research Alert: Observational Study in Female Carriers of DMD/BMD and Their Biological Children
Researchers at Natera are seeking female carriers of Duchenne/Becker muscular dystrophy (DMD/BMD) and their affected or unaffected biological children for an observational study (DYADS study). This study will collect blood…
Research Network Supports Limb-Girdle Muscular Dystrophy Treatment Development
How MDA is supporting a research consortium aimed at boosting clinical trial readiness for developing LGMD treatments.
Tags: Clinical Trials, Drug Development, Featured Content, Gene Therapy, Genetic Testing, Grants, Research
Clinical Research Alert: Phase 2 Study of NMD670 in Adults with Generalized Myasthenia Gravis (gMG)
Researchers at NMD Pharma A/S are working to better understand generalized myasthenia gravis (gMG) and study efficacy of a potentially new treatment. The study People who have generalized myasthenia gravis (gMG)…
Rare Disease Day: Momentum in Neuromuscular Diseases is Building, but Progress Depends on Sustained Investment
Every year on Rare Disease Day, communities around the world come together to shine a light on conditions that are too often overlooked or underfunded. Historically, rare diseases have been…