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In this Quest Podcast episode, we chat with internationally recognized fashion designer Izzy Camilleri, a true pioneer in adaptive fashion. She shares how her successful career in high-end fashion took…

X-linked myotubular myopathy (XLMTM) is a rare, inherited neuromuscular condition that primarily affects infant males. It is one of the most severe forms within a group of disorders called centronuclear…

What should you do if you have a variant of unknown significance in genetic testing results? Hear from experts in the neuromuscular field.

Tips for participating in neuromuscular clinical trials and research studies, from MDA community members who have been there.

Follow these steps to appeal insurance denials for gene therapy, or any neuromuscular disease treatment, and improve your chances for approval.

Michio Hirano, MD, answers questions about TK2d, a rare mitochondrial myopathy with a new therapy approved by the FDA.

RNA therapies offer new hope for neuromuscular diseases, targeting faulty proteins without permanently altering DNA.

Caroline LeMay, a Harvard graduate living with a disability, knows the importance of education to achieve her dreams.

Tracking research updates and breakthroughs that help accelerate treatments and cures across MDA diseases.

Discoveries presented at the MDA Clinical & Scientific Conference can shape the future of neuromuscular care.