Clinical Trials

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Clinical Trial Alert: Amicus Therapeutics Seeks Participants for a Phase 3 Late-Onset Pompe Disease Study

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FDA Accepts Sarepta Therapeutics’ New Drug Application (NDA) for Golodirsen to Treat DMD Amenable to Exon 53 Skipping

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Long-Term Results of Extension Study Validate Surgery as a Treatment for Myasthenia Gravis

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Solid Biosciences Announces Preliminary Results of DMD Gene Therapy Trial

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Catalyst Pharmaceuticals Announces Positive Results from Phase 2b Trial of Firdapse in Patients with Muscle-Specific Kinase Antibody Positive Myasthenia Gravis (MuSK-MG)

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Clinical Trial Alert: Brainstorm Cell Therapeutics Seeks Participants for a Phase 3 ALS Study

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FDA Awards Fast Track Status to RNS60, Revalesio’s Investigational Therapy for ALS

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Clinical Trial Alert: Orphazyme Seeks Participants for a Phase 3 ALS Study

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Clinical Trial Alert: Catabasis Seeks Participants for a Phase 3 DMD Study

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Wave Life Sciences Announces Phase 2/3 Duchenne Muscular Dystrophy Clinical Trial of Suvodirsen (WVE-210201) Selected for FDA Complex Innovative Trial Designs Pilot Program