Clinical Trials

Featured Article

MDA’s 2020 Clinical Scientific Conference Trial News and Updates

By MDA Staff | May 15, 2020
Featured Article

Pompe Disease Treatment Is Moving Forward

By MDA Staff | May 15, 2020
Blog Post

Clinical Trials During COVID-19: What We Need From the FDA

By Paul Melmeyer | May 12, 2020
Blog Post

Acceleron Pharma Announces Discontinuation of Clinical Trials Program for CMT

By Jeanene Swanson | March 18, 2020
Blog Post

NS Pharma Launches Expanded Access Program for Viltolarsen

By Jeanene Swanson | March 9, 2020
Illustration of DNA
Blog Post

FDA Accepts NS Pharma’s NDA for Viltolarsen for the Treatment of DMD Amenable to Exon 53 Skipping

By Jeanene Swanson | February 26, 2020
Blog Post

MDA’s New Chief Research Officer Sharon Hesterlee Shares Vision for the Future

By Jeanene Swanson | February 21, 2020
Blog Post

Roche Genentech Announces Positive Results from Pivotal Study of Risdiplam in SMA Type 1

By Jeanene Swanson | January 31, 2020

Clinical Trial Alert: LGMD2E Participants Sought for a Phase 1/2a Gene Delivery Study

By MDA Staff | January 29, 2020
Blog Post

Clinical Trial Alert: Individuals with SMA Type 3 Sought for a Phase 2 Study

By MDA Staff | January 27, 2020