News

Read the latest news about issues affecting the neuromuscular disease community.

Blog Post

Roche Genentech Announces Positive Results from Pivotal Study of Risdiplam in SMA Type 1

By Jeanene Swanson | January 31, 2020

Clinical Trial Alert: LGMD2E Participants Sought for a Phase 1/2a Gene Delivery Study

By MDA Staff | January 29, 2020
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Clinical Trial Alert: Individuals with SMA Type 3 Sought for a Phase 2 Study

By MDA Staff | January 27, 2020
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Antisense Therapeutics Announces Positive Results from Phase 2 Study of ATL1102 in DMD

By Jeanene Swanson | January 24, 2020
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MDA Awards More Than $1 Million in Venture Philanthropy Funding to AavantiBio to Develop Gene-Targeting Therapy for Friedreich’s Ataxia

By Jeanene Swanson | January 13, 2020
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Mallinckrodt Pharmaceuticals Releases Statement to DMD Community Announcing Discontinuation of Clinical Trials Program for DMD

By MDA Staff | December 20, 2019
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FDA Approves ITF Pharma’s Tiglutik via PEG Tube for the Treatment of ALS

By Jeanene Swanson | December 20, 2019
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Amylyx Pharmaceuticals Announces Positive Results from Phase 2 Study of AMX0035 for Treatment of ALS

By Jeanene Swanson | December 19, 2019
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Santhera Pharmaceuticals Announces Publication of Positive Long-Term Results from Retrospective Study of Idebenone in DMD

By Jeanene Swanson | December 18, 2019
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Solid Biosciences Releases Letter to DMD Community Announcing Update on IGNITE DMD Trial, Resolution of Serious Adverse Event

By MDA Staff | December 18, 2019