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Meet the 2026 MDA Legacy and Momentum award winners who are making a lasting impact on research and care for the neuromuscular community.

Researchers at Natera are seeking female carriers of Duchenne/Becker muscular dystrophy (DMD/BMD) and their affected or unaffected biological children for an observational study (DYADS study). This study will collect blood…

How MDA is supporting a research consortium aimed at boosting clinical trial readiness for developing LGMD treatments.

Researchers at NMD Pharma A/S are working to better understand generalized myasthenia gravis (gMG) and study efficacy of a potentially new treatment. The study People who have generalized myasthenia gravis (gMG)…

Every year on Rare Disease Day, communities around the world come together to shine a light on conditions that are too often overlooked or underfunded. Historically, rare diseases have been…

In this Quest Podcast episode, we chat with internationally recognized fashion designer Izzy Camilleri, a true pioneer in adaptive fashion. She shares how her successful career in high-end fashion took…

X-linked myotubular myopathy (XLMTM) is a rare, inherited neuromuscular condition that primarily affects infant males. It is one of the most severe forms within a group of disorders called centronuclear…

What should you do if you have a variant of unknown significance in genetic testing results? Hear from experts in the neuromuscular field.

Tips for participating in neuromuscular clinical trials and research studies, from MDA community members who have been there.

Follow these steps to appeal insurance denials for gene therapy, or any neuromuscular disease treatment, and improve your chances for approval.