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Tips for participating in neuromuscular clinical trials and research studies, from MDA community members who have been there.

Follow these steps to appeal insurance denials for gene therapy, or any neuromuscular disease treatment, and improve your chances for approval.

Michio Hirano, MD, answers questions about TK2d, a rare mitochondrial myopathy with a new therapy approved by the FDA.

RNA therapies offer new hope for neuromuscular diseases, targeting faulty proteins without permanently altering DNA.

Caroline LeMay, a Harvard graduate living with a disability, knows the importance of education to achieve her dreams.

Tracking research updates and breakthroughs that help accelerate treatments and cures across MDA diseases.

Discoveries presented at the MDA Clinical & Scientific Conference can shape the future of neuromuscular care.

MDA community members share meaningful moments and everyday milestones from the past year.

Trained sports broadcaster Michael Chamberlain has spent his career showing that people with disabilities belong in the sports world.

New gene sequencing technologies mean better genetic testing, fewer delays in diagnosis, and more access to gene therapies.