Clinical Trials

Blog Post

Sarepta Therapeutics Announces Positive Results from the SRP-9003 Gene Therapy Trial to Treat LGMD2E

By Sujatha Gurunathan | June 11, 2020
Blog Post

ReveraGen BioPharma Announces Completion of Vamorolone Study in 41 DMD Patients

By Sujatha Gurunathan | June 8, 2020
Blog Post

NS Pharma Announces Positive Results from Phase 2 Study of Viltolarsen in DMD

By Sujatha Gurunathan | June 3, 2020
Blog Post

Pfizer Announces Positive Results from Phase 1b Study of PF-06939926 for Treatment of DMD

By Sujatha Gurunathan | June 1, 2020
Blog Post

Orphazyme Announces FDA Fast Track Designation for Development of Arimoclomol for Treatment of ALS

By Sujatha Gurunathan | May 26, 2020
Featured Article

MDA’s 2020 Clinical Scientific Conference Trial News and Updates

By MDA Staff | May 15, 2020
Featured Article

Pompe Disease Treatment Is Moving Forward

By MDA Staff | May 15, 2020
Blog Post

Clinical Trials During COVID-19: What We Need From the FDA

By Paul Melmeyer | May 12, 2020
Blog Post

Acceleron Pharma Announces Discontinuation of Clinical Trials Program for CMT

By Jeanene Swanson | March 18, 2020
Blog Post

NS Pharma Launches Expanded Access Program for Viltolarsen

By Jeanene Swanson | March 9, 2020