Clinical Trials

Blog Post

FDA Approves Sarepta Therapeutics’ Amondys 45 for Treatment of DMD Amenable to Skipping Exon 45

By Sujatha Gurunathan | February 25, 2021
Blog Post

Clinical Trial Alert: Phase 3 Study of Rozanolixizumab in Individuals With Generalized Myasthenia Gravis

By MDA Staff | February 23, 2021
Blog Post

MDA’s 2021 Advocacy Plan

By Mark Fisher | February 2, 2021
Blog Post

Research Study Alert: LGMD2I Natural History Study

By MDA Staff | January 25, 2021
Featured Article

Clinical Trials During COVID 19

By MDA Staff | December 4, 2020
Featured Article

The Search for Inclusion Body Myositis Treatment

By MDA Staff | December 4, 2020
Blog Post

Once a Wild Idea, Successful First-Generation Exon-Skipping Therapies Pave the Way for Personalized Treatments

By Sujatha Gurunathan | November 17, 2020
Blog Post

Scholar Rock Announces Positive Results from Interim Analysis of TOPAZ Phase 2 Study of SRK-015 to Treat SMA

By Sujatha Gurunathan | October 28, 2020
Blog Post

Amylyx Announces More Results from Study of AMX0035 to Treat ALS

By Sujatha Gurunathan | October 19, 2020
Featured Article

Expanding Access to Genetic Testing

By Donna Albrecht | August 14, 2020