Research

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Clinical Trial Alert: Amicus Therapeutics Seeks Participants for a Phase 3 Late-Onset Pompe Disease Study

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Clinical Trial Alert: Momenta Pharmaceuticals Seeks Participants for a Phase 2 Myasthenia Gravis Study

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NS Pharma Submits New Drug Application to FDA for Viltolarsen to Treat DMD Amenable to Exon 53 Skipping

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At a Cedars-Sinai Care Center, Dr. Robert Baloh Looks Under — and Ahead of — the Microscope for CMT and ALS

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Five Questions with LGMD Researcher Martin Childers

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MDA Awards Clinical Research Network Grant to CMT Researcher Michael Shy for Inherited Neuropathies Consortium

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In a Letter to the Duchenne Community, Santhera Announces Positive Results of Phase 2 Vamorolone Study, EMA’s Review of Puldysa to Treat Symptoms of DMD

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Clinical Trial Alert: Italfarmaco Seeks Participants for a Phase 3 DMD Study

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Five Questions with Friedreich’s Ataxia Researcher Sanjay Bidichandani

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Researcher with CMT Awarded MDA Funding to Discover Rare Variants for Multiple Neuromuscular Diseases