Clinical Trials

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Capricor Therapeutics Announces Positive Interim Results from Phase 2 Study of CAP-1002 to Treat DMD

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MDA Grants Charles Thornton More Than $1 Million in New Funding to Continue Supporting the Myotonic Dystrophy Clinical Research Network

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ReveraGen Presents Positive Interim Results from Phase 2 Extension Study of Vamorolone to Treat DMD in Young Boys

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NS Pharma Submits New Drug Application to FDA for Viltolarsen to Treat DMD Amenable to Exon 53 Skipping

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In a Letter to the Duchenne Community, Santhera Announces Positive Results of Phase 2 Vamorolone Study, EMA’s Review of Puldysa to Treat Symptoms of DMD

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Clinical Trial Alert: Italfarmaco Seeks Participants for a Phase 3 DMD Study

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Participants Needed for a Pilot Study of a New Diagnostic Device

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Biogen Announces Positive Long-Term Results from Phase 2 Study of Spinraza to Treat SMA in Pre-Symptomatic Infants

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The ALS Association, ALS Finding A Cure, and MDA Co-Fund Clinical Trial Grant to Study Restoring Immune System Function to Treat ALS

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Scholar Rock Announces Positive Results from Phase 1 Study of SRK-015 to Treat SMA