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While there are still challenges to researching therapies for ultra-rare neuromuscular diseases, many in the field see reasons for hope

Chris Benyo With the help of Team Momentum, a racing wheelchair connected and impacted multiple MDA families

Releasing my first album took a lifetime of imagination and determination

Finding accessible employment in the work-from-home era

Access Workshop helps families overcome barriers to school

Educating others about disability can be a heavy lift, but advocates in our community say it’s worth the effort

These advocates have learned to recognize and call out ableism where they see it

Researchers at Cumberland Pharmaceuticals Inc. are seeking boys and men living with Duchenne muscular dystrophy (DMD) to participate in a phase 2 clinical trial to evaluate the safety, efficacy, and duration…

Researchers at Astellas Pharma Inc. are seeking individuals living with primary mitochondrial myopathy (PMM) to participate in a phase 2/3 clinical trial and open-label extension to evaluate safety, tolerability and preliminary…

On Aug. 6, the US Food and Drug Administration (FDA) granted accelerated marketing approval to avalglucosidase alfa (Nexviazyme) for the treatment of people 1 year of age and older living…