Archives

On June 22, the US Food and Drug Administration (FDA) granted accelerated approval of ELEVIDYS (delandistrogene moxeparvovec-rokl) for the treatment of ambulatory pediatric patients aged 4 through 5 years with Duchenne…

Packing for vacation when you live with a disability requires a little extra planning and preparation. Travel often demands additional considerations to provide easy access to essentials and ensure that…

On June 20, the US Food and Drug Administration (FDA) granted marketing approval of subcutaneous (SC) Vyvgart Hytrulo (efgartigimod alfa and hyaluronidase-qvfc) for the treatment of generalized myasthenia gravis (gMG)…

Janet Rodenhouse and her sisters have a lot in common. The seven women share a love for dancing, a deep appreciation of finding humor in all things, and a strong…

Dear Muscular Dystrophy, MDA National Ambassador Amy Shinneman At times you dazzle me, showing me the heights of human love and kindness, and at other times you take me to…

Charlotte and Elizabeth Madole. For many individuals living with a rare disease, the road to diagnosis can be extremely challenging, especially when it involves two co-existing diseases where two parts…

Researchers at the University of Florida are seeking adult males living with Becker muscular dystrophy (BMD) to participate in a three-year natural history study. The objective of this observational study is to…

Quest Media is an innovative adaptive lifestyle platform from MDA. With the power of this platform, we foster awareness and empowerment and have important conversations with experts, thought leaders, and…

Nevin Steiner and his children, Abbott and Laurel. Being a father is one of the most rewarding things in life. I have two children, Abbott (6) and Laurel (3). Add having…

As MDA welcomes back a busy schedule of in-person events this year, there are a myriad of ways that individuals can come together and reap the benefits of time well…